Target gene | Vector | Modification |
---|
CFTR[7]§ | CH242-248P18 (>100 kb) | ATG-STOP |
DMD[42]§ | CH242-9G11 (>100 kb) | Δ exon 52 |
GGTA1
| CH242-21Â F3 (>100Â kb) | ATG-STOP |
APC[64]§ | 12.5 kb | STOP |
KRAS
| 13.5Â kb | Point mutation |
JAK3
| 13.8 kb | Δ exon 2-5 |
- § See indicated references.