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Table 2 List of the double-stranded DNA fragments used to target the mutated genes

From: A comparison of synthetic oligodeoxynucleotides, DNA fragments and AAV-1 for targeted episomal and chromosomal gene repair

Name

Size

Sequence

200 dsDNA Ctr

195 bp

5'-CGGCA..//..TGGCAGAAGCTATGAAACGATAGGGGCTGAATACAAATCACAGAA..//..TGTTG-3'

3'-GCCGT..//..ACCGTCTTCGATACTTTGCTATCCCCGACTTATGTTTAGTGTCTT..//..CAAGC-5'

500 dsDNA Ctr

494 bp

5'-CACGT..//..TGGCAGAAGCTATGAAACGATAGGGGCTGAATACAAATCACAGAA..//..GTTCG-3'

3'-GTGCA..//..ACCGTCTTCGATACTTTGCTATCCCCGACTTATGTTTAGTGTCTT..//..CAAGC-5'

1000 dsDNA Ctr

980 bp

5'-TACAA..//..TGGCAGAAGCTATGAAACGATAGGGGCTGAATACAAATCACAGAA..//..AGATT-3'

3'-ATGTT..//..ACCGTCTTCGATACTTTGCTATCCCCGACTTATGTTTAGTGTCTT..//..TCTAA-5'

2200 dsDNA Ctr

2133 bp

5'-AAATG..//..TGGCAGAAGCTATGAAACGATAGGGGCTGAATACAAATCACAGAA..//..ACATT-3'

3'-TTTAC..//..ACCGTCTTCGATACTTTGCTATCCCCGACTTATGTTTAGTGTCTT..//..TGTAA-5'

200 dsDNA Rep

195 bp

5'-CGGCA..//..TGGCAGAAGCTATGAAACGATATGGGCTGAATACAAATCACAGAA..//..TGTTG-3'

3'-GCCGT..//..ACCGTCTTCGATACTTTGCTATACCCGACTTATGTTTAGTGTCTT..//..CAAGC-5'

500 dsDNA Rep

494 bp

5'-CACGT..//..TGGCAGAAGCTATGAAACGATATGGGCTGAATACAAATCACAGAA..//..GTTCG-3'

3'-GTGCA..//..ACCGTCTTCGATACTTTGCTATACCCGACTTATGTTTAGTGTCTT..//..CAAGC-5'

1000 dsDNA Rep

980 bp

5'-TACAA..//..TGGCAGAAGCTATGAAACGATATGGGCTGAATACAAATCACAGAA..//..AGATT-3'

3'-ATGTT..//..ACCGTCTTCGATACTTTGCTATACCCGACTTATGTTTAGTGTCTT..//..TCTAA-5'

2200 dsDNA Rep

2133 bp

5'-AAATG..//..TGGCAGAAGCTATGAAACGATATGGGCTGAATACAAATCACAGAA..//..ACATT-3'

3'-TTTAC..//..ACCGTCTTCGATACTTTGCTATACCCGACTTATGTTTAGTGTCTT..//..TGTAA-5'

GFP 700 dsDNA Ctr

732 bp

5'-AAATG..//..CAAGCTGCCCGTGCCCTAGCCAACCCTCGTGACCA..//..GAGCA-3'

3'-TTTAC..//..GTTCGACGGGCACGGGATCGGTTGGGAGCACTGGT..//..CTCGT-5'

GFP 700 dsDNA Rep

732 bp

5'-AAATG..//..CAAGCTGCCCGTGCCCTGGCCAACCCTCGTGACCA..//..GAGCA-3'

3'-TTTAC..//..GTTCGACGGGCACGGGACCGGTTGGGAGCACTGGT..//..CTCGT-5'

  1. Ctr, non-correcting control fragment; Rep, repair fragment; GFP, green fluorescent protein; in bold, position of the base to correct.